Polycystic Kidney Disease in Children: The Current Status and the Next Horizon
Cadnapaphornchai M, Dell K, Gimpel C, Guay-Woodford L, Gulati A, Hartung E, Liebau M, Mallett A, Marlais M, Mekahli D, Piccirilli A, Seeman T, Tindal K, Winyard P. Polycystic Kidney Disease in Children: The Current Status and the Next Horizon. American Journal Of Kidney Diseases 2025 PMID: 40113156, DOI: 10.1053/j.ajkd.2025.01.022.Peer-Reviewed Original ResearchAutosomal recessive polycystic kidney diseaseAutosomal dominant polycystic kidney diseasePolycystic kidney diseaseKidney diseaseFetal lifePathogenic mechanismsUrinary concentrating defectProgressive chronic kidney diseaseRecessive polycystic kidney diseaseDominant polycystic kidney diseaseChronic kidney diseaseAdult-onset diseaseDiagnostic modalitiesConcentrating defectPortfolio of clinical trialsTherapeutic managementClinical trialsInherited disorderBurden of diseaseClinical assessmentKidney cystsTherapeutic targetCilia dysfunctionAge groupsDisease
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